An Open-label, Multi-center, Expanded Access Study of Pasireotide s.c. in Patients With Cushing's Disease (MACS1599)

This study is currently recruiting participants.
Verified March 2013 by Novartis
Sponsor:
Information provided by (Responsible Party):
Novartis ( Novartis Pharmaceuticals )
ClinicalTrials.gov Identifier:
NCT01582061
First received: April 12, 2012
Last updated: March 22, 2013
Last verified: March 2013
  Purpose

This study will document the safety and efficacy of pasireotide s.c. in patients with Cushing's disease.


Condition Intervention Phase
Cushing's Disease
Drug: Pasireotide sub-cutaneous formulation
Phase 3

Novartis Pharmaceuticals has indicated that access to an investigational treatment associated with this study is available outside the clinical trial.  

Study Type: Interventional
Study Design: Allocation: Non-Randomized
Endpoint Classification: Safety Study
Intervention Model: Single Group Assignment
Masking: Open Label
Primary Purpose: Treatment
Official Title: An Open-label, Multi-center, Expanded Access Study of Pasireotide s.c. in Patients With Cushing's Disease (Seascape)

Resource links provided by NLM:


Further study details as provided by Novartis:

Primary Outcome Measures:
  • Proportion of patients having a drug-related adverse event that is recorded as grade 3 or 4 or as a serious adverse event [ Time Frame: Week 0, 1, 2, 3, 4, 8, 12, 16, 20, 24, 36, 48 ] [ Designated as safety issue: Yes ]

Secondary Outcome Measures:
  • Proportion of patients with mean Urinary Free Cortisol (UFC) ≤ Upper Limit of Normal (ULN) [ Time Frame: Baseline, week 12, 24 and 48 ] [ Designated as safety issue: No ]
  • Proportion of patients achieving a reduction of mean UFC ≥ 50% [ Time Frame: Baseline, week 12, 24 and 48 ] [ Designated as safety issue: No ]
  • Change in Cushing's disease clinical signs and symptoms [ Time Frame: Baseline, week 12, 24 and 48 ] [ Designated as safety issue: No ]
  • Change in Cushing Quality of Life and Work Productivity and Activity Impairment-General Health (WPAI-GH) scores [ Time Frame: Baseline, week 12, 24 and 48 ] [ Designated as safety issue: No ]
  • Change in GH and IGF-I values [ Time Frame: Baseline, week 12, 24 and 48 ] [ Designated as safety issue: No ]

Estimated Enrollment: 300
Study Start Date: August 2011
Estimated Study Completion Date: January 2014
Estimated Primary Completion Date: January 2014 (Final data collection date for primary outcome measure)
Arms Assigned Interventions
Experimental: Pasireotide sub-cutaneous formulation
Pasireotide will be administered twice a day until pasireotide is approved and reimbursed for commercial use in each respective country or until 31DEC13, whichever comes first
Drug: Pasireotide sub-cutaneous formulation
Pasireotide will be administered twice a day until pasireotide is approved and reimbursed for commercial use in each respective country or until 31DEC13, whichever comes first
Other Name: SOM230 sub-cutaneous formulation

  Eligibility

Ages Eligible for Study:   18 Years and older
Genders Eligible for Study:   Both
Accepts Healthy Volunteers:   No
Criteria

Inclusion criteria:

  1. Patients with confirmed diagnosis of Cushing's disease as evidenced by

    • mean urinary free cortisol of three 24-hour urine samples collected during the 2-week screening period above the upper limit of the laboratory normal range
    • morning plasma adrenocorticotropic hormone (ACTH) within the normal or above normal range
    • either Magnetic Resonance Imaging (MRI) confirmation of pituitary adenoma (greater than or equal to 0.6 cm), or inferior petrosal sinus gradient >3 after corticotrophin-releasing hormone (CRH) stimulation for those patients with a microadenoma less than 0.6 cm, or for patients who have had prior pituitary surgery, histopathology confirming an ACTH staining adenoma.
  2. Patients with de novo Cushing's disease must not be considered as candidates for pituitary surgery (i.e. poor surgical candidates, surgically unapproachable tumors, patients with no visible pituitary tumor, patients who refuse to have surgical treatment)
  3. Karnofsky performance status >60 (i.e. requires occasional assistance, but is able to care for most of his personal needs)

Exclusion criteria:

  1. Radiotherapy of the pituitary <4 weeks before screening or patient who has not recovered from side effects
  2. Patients with compression of the optic chiasm causing acute clinically significant visual field defect
  3. Patients with Cushing's syndrome due to ectopic ACTH secretion
  4. Patients with hypercortisolism secondary to adrenal tumors or nodular (primary) bilateral adrenal hyperplasia
  5. Patients who have undergone major surgery within 1 month prior to screening
  6. Patients with symptomatic cholelithiasis
  7. Patients who have clinically significant impairment in cardiovascular function or are at risk thereof.

Other protocol-defined inclusion/exclusion criteria may apply

  Contacts and Locations
Please refer to this study by its ClinicalTrials.gov identifier: NCT01582061

Contacts
Contact: Novartis Pharmaceuticals 1-888-669-6682
Contact: Novartis Pharmaceuticals

  Hide Study Locations
Locations
United States, Alabama
University of Alabama at Birmingham Not yet recruiting
Birmingham, Alabama, United States, 35294
Contact     +1 205 934 2130        
Principal Investigator: Tom Brooks Vaughan            
United States, Arizona
Panda Medical Associates/Clin TriCo Recruiting
Peoria, Arizona, United States, 85381
Contact: Cyndi Sepico         cyndi@clintrico.com    
Principal Investigator: Chioma Iweha            
St. Joseph's Hospital & Medical Center St Joes Recruiting
Phoenix, Arizona, United States, 85013
Contact: Emily Khoury     602-406-3614     emily.khoury@chw.edu    
Principal Investigator: Laura Knecht            
United States, Arkansas
University of Arkanasas for Medical Sciences Withdrawn
Little Rock, Arkansas, United States, 72205
United States, California
Cedars Sinai Medical Center Withdrawn
Los Angeles, California, United States, 90048
University of California at Los Angeles UCLA Tiverton Recruiting
Los Angeles, California, United States, 90095
Contact: Brittany Sumerel     310-825-5874     bsumerel@mednet.ucla.edu    
Principal Investigator: Anthony P. Heaney            
San Diego Endocrine & Medical Clinic Recruiting
San Diego, California, United States, 92108
Contact     619-220-7990        
Principal Investigator: Georges M. Argoud            
University of California San Francisco Withdrawn
San Francisco, California, United States, 94143-0326
John Wayne Cancer Institute Not yet recruiting
Santa Monica, California, United States, 90404
Contact     310-829-8858        
Principal Investigator: Daniel F. Kelly            
Stanford Cancer Center Withdrawn
Stanford, California, United States, 94305
LA Biomedical Research at Harbor UCLA Medical Center Recruiting
Torrance, California, United States, 90502
Contact     310-222-4060        
Principal Investigator: Ronald Swerdloff            
United States, Colorado
University of Colorado Withdrawn
Aurora, Colorado, United States, 80045
United States, District of Columbia
George Washington University Medical Center Not yet recruiting
Washington, District of Columbia, United States, 20037
Contact     202-741-2293        
Principal Investigator: Zachary Litvak            
United States, Georgia
Emory University School of Medicine Not yet recruiting
Atlanta, Georgia, United States, 30322
Contact     404-727-5725        
Principal Investigator: Adriana Ioachimescu            
United States, Illinois
Northwestern University Not yet recruiting
Chicago, Illinois, United States, 60611
Contact     312-908-1299        
Principal Investigator: Mark Molitch            
John H. Stroger, K., Hospital of Cook County Recruiting
Chicago, Illinois, United States, 60612
Contact     312-864-0539        
Principal Investigator: Leon Fogelfeld            
United States, Maryland
U of Maryland Medical Center Not yet recruiting
Baltimore, Maryland, United States, 21201
Contact     410-328-0303        
Principal Investigator: Kashif Munir            
United States, Massachusetts
Tufts Medical Center Not yet recruiting
Boston, Massachusetts, United States, 02111
Contact     617-636-0710        
Principal Investigator: Ronald M. Lechan            
Tufts Medical Center Withdrawn
Boston, Massachusetts, United States, 02111
United States, Michigan
University of Michigan Medical Center Withdrawn
Ann Arbor, Michigan, United States, 48109-0922
Wayne State University Withdrawn
Detroit, Michigan, United States, 48201
United States, Missouri
Washington University Not yet recruiting
St. Louis, Missouri, United States, 63110
Contact     341-362-3181        
Principal Investigator: Julie Silverstein            
United States, Nebraska
Diabetes and Endocrinology Associates, PC Recruiting
Omaha, Nebraska, United States, 68131
Contact     402-561-2665        
Principal Investigator: Claire H. Baker            
U of Nebraska Medical Center Not yet recruiting
Omaha, Nebraska, United States, 68198
Contact     402-559-4341        
Principal Investigator: Andjela Drincic            
United States, New Mexico
University of New Mexico Hospital UNM Not yet recruiting
Albuquerque, New Mexico, United States, 87106
Contact: Lisa Toelle     505-272-1663     ljtoelle@salud.unm.edu    
Principal Investigator: Kathleen Colleran            
United States, New York
Mount Sinai School of Medicine Not yet recruiting
New York, New York, United States, 10029
Contact     212-659-8833        
Principal Investigator: Eliza B. Geer            
University of Rochester Medical Center Withdrawn
Rochester, New York, United States, 14642
United States, Ohio
Cleveland Clinic Foundation Withdrawn
Cleveland, Ohio, United States, 44195
Toledo Clinic Not yet recruiting
Toledo, Ohio, United States, 43623
Contact     419-479-5560        
Principal Investigator: Ian Elliot            
United States, Oregon
Oregon Health & Science University OHSU 5 Recruiting
Portland, Oregon, United States, 97239
Contact: Sarah Colton     503-494-9546     colton@ohsu.edu    
Principal Investigator: Maria Fleseriu            
United States, Pennsylvania
Temple University Not yet recruiting
Philadelphia, Pennsylvania, United States, 19140
Contact     215-707-5477        
Principal Investigator: Elias Siraj            
University of Pennsylvania Medical Center Univ Penn Recruiting
Philadephia, Pennsylvania, United States, 19104
Contact: Invest Drug     215-898-5664     rockwelk@mail.med.upenn.edu    
Principal Investigator: Peter J. Snyder            
Allegheny Endocrinology Associates Recruiting
Pittsburgh, Pennsylvania, United States, 15212
Contact     412-359-5143        
Principal Investigator: Murray B. Gordon            
United States, Rhode Island
Rhode Island Hospital Not yet recruiting
Providence, Rhode Island, United States, 02903
Contact     401-444-5901        
Principal Investigator: Geetha Gopalakrishnan            
United States, South Carolina
Medical University of South Carolina Withdrawn
Charleston, South Carolina, United States, 29406
United States, Tennessee
Mid South Endocrine Associates Recruiting
Nashville, Tennessee, United States, 37203
Contact     615-329-5029        
Principal Investigator: Terri Jerkins            
Vanderbilt University Medical Center Not yet recruiting
Nashville, Tennessee, United States, 37212
Contact     615-936-0067        
Principal Investigator: Andrea Utz            
United States, Texas
University of Texas Southwestern Medical Center UT southwest Withdrawn
Dallas, Texas, United States, 75390-8527
Baylor College of Medicine Not yet recruiting
Houston, Texas, United States, 77030
Contact     713-793-7664        
Principal Investigator: Susan L. Samson            
United States, Washington
Swedish Cancer Institute Swedish Cancer Institute (SC) Not yet recruiting
Seattle, Washington, United States, 98104
Contact: Becky Wood     206-320-7115     becky.wood@swedish.org    
Principal Investigator: Frances Broyles            
Brazil
Novartis Investigative Site Recruiting
Fortaleza, CE, Brazil, 60155-290
Novartis Investigative Site Recruiting
Joinville, SC, Brazil, 89201260
Novartis Investigative Site Withdrawn
São Paulo, SP, Brazil, 01401-901
Novartis Investigative Site Recruiting
São Paulo, SP, Brazil, 05403-000
Novartis Investigative Site Recruiting
São Paulo, SP, Brazil, 04029-000
Czech Republic
Novartis Investigative Site Recruiting
Prague 2, Czech Republic, 120 00
Egypt
Novartis Investigative Site Not yet recruiting
Alexandria, Egypt
Novartis Investigative Site Not yet recruiting
Mansoura, Egypt
Germany
Novartis Investigative Site Completed
Aachen, Germany, 52074
Novartis Investigative Site Completed
Augsburg, Germany, 86150
Novartis Investigative Site Withdrawn
Berlin, Germany, 12200
Novartis Investigative Site Withdrawn
Berlin, Germany, 10117
Novartis Investigative Site Withdrawn
Berlin, Germany, 12159
Novartis Investigative Site Terminated
Berlin, Germany, 10098
Novartis Investigative Site Completed
Berlin, Germany, 13353
Novartis Investigative Site Withdrawn
Bielefeld, Germany, 33604
Novartis Investigative Site Withdrawn
Dortmund, Germany, 44137
Novartis Investigative Site Withdrawn
Duesseldorf, Germany, 40225
Novartis Investigative Site Completed
Erlangen, Germany, 91054
Novartis Investigative Site Withdrawn
Essen, Germany, 45147
Novartis Investigative Site Terminated
Frankfurt, Germany, 60329
Novartis Investigative Site Completed
Frankfurt, Germany, 60590
Novartis Investigative Site Active, not recruiting
Göttingen, Germany, D-37075
Novartis Investigative Site Completed
Hamburg, Germany, 22559
Novartis Investigative Site Withdrawn
Hannover, Germany, 30625
Novartis Investigative Site Terminated
Heidelberg, Germany, 69120
Novartis Investigative Site Withdrawn
Kiel, Germany, 24105
Novartis Investigative Site Withdrawn
Köln, Germany, 50924
Novartis Investigative Site Terminated
Leipzig, Germany, 04103
Novartis Investigative Site Withdrawn
Lübeck, Germany, 23538
Novartis Investigative Site Completed
Mainz, Germany, D-55101
Novartis Investigative Site Terminated
Marburg, Germany, 35039
Novartis Investigative Site Completed
Muenchen, Germany, 80804
Novartis Investigative Site Withdrawn
München, Germany, 80336
Novartis Investigative Site Withdrawn
Nuernberg, Germany, 90491
Novartis Investigative Site Terminated
Oldenburg, Germany, 26122
Novartis Investigative Site Completed
Würzburg, Germany, 97080
Greece
Novartis Investigative Site Recruiting
Athens, Greece, GR 156 69
Novartis Investigative Site Recruiting
Athens - GR, Greece, 10676
Novartis Investigative Site Recruiting
Heraklion/ Crete, Greece, 710 00
Novartis Investigative Site Recruiting
Larissa, Greece, 41110
Novartis Investigative Site Recruiting
Pireas, Greece, 18537
Novartis Investigative Site Not yet recruiting
Thessaloniki, Greece, GR 54635
Novartis Investigative Site Not yet recruiting
Thessaloniki, Greece, GR 55132
Novartis Investigative Site Recruiting
Thessaloniki, Greece, GR 546 39
Korea, Republic of
Novartis Investigative Site Recruiting
Seoul, Korea, Korea, Republic of, 135-710
Novartis Investigative Site Recruiting
Seoul, Korea, Republic of, 120-752
Novartis Investigative Site Recruiting
Seoul, Korea, Republic of, 130-702
Lebanon
Novartis Investigative Site Recruiting
Beirut, Lebanon
Netherlands
Novartis Investigative Site Completed
Enschede, Netherlands, 7513 ER
Novartis Investigative Site Withdrawn
Leiden, Netherlands, 2300 RC
Romania
Novartis Investigative Site Recruiting
Bucharest, Romania, 011461
Novartis Investigative Site Recruiting
Bucuresti, Romania
Novartis Investigative Site Recruiting
Cluj, Romania, 400006
Novartis Investigative Site Recruiting
Iasi, Romania, 700106
Russian Federation
Novartis Investigative Site Not yet recruiting
Krasnoyarsk, Russian Federation, 660022
Novartis Investigative Site Not yet recruiting
Moscow, Russian Federation, 129110
Novartis Investigative Site Not yet recruiting
Samara, Russian Federation, 443095
Spain
Novartis Investigative Site Recruiting
Cordoba, Andalucia, Spain, 14004
Novartis Investigative Site Recruiting
Sevilla, Andalucia, Spain, 41009
Novartis Investigative Site Recruiting
Granada, Andalucía, Spain, 18003
Novartis Investigative Site Withdrawn
Leon, Castilla y Leon, Spain, 24071
Novartis Investigative Site Recruiting
Badalona, Catalunya, Spain, 08916
Novartis Investigative Site Recruiting
Valencia, Comunidad Valenciana, Spain, 46014
Novartis Investigative Site Recruiting
La Coruna, Galicia, Spain, 15006
Novartis Investigative Site Recruiting
Orense, Galicia, Spain, 32005
Novartis Investigative Site Recruiting
Palma De Mallorca, Islas Baleares, Spain, 07120
Novartis Investigative Site Recruiting
Baracaldo, País Vasco, Spain, 48903
Novartis Investigative Site Withdrawn
Madrid, Spain, 28046
Novartis Investigative Site Recruiting
Madrid, Spain, 28034
Novartis Investigative Site Recruiting
Madrid, Spain, 28040
Novartis Investigative Site Recruiting
Pontevedra, Spain, 36071
Novartis Investigative Site Recruiting
Valencia, Spain, 46026
Thailand
Novartis Investigative Site Recruiting
Bangkok, Thailand, 10330
Novartis Investigative Site Recruiting
Songkla, Thailand, 90110
Sponsors and Collaborators
Novartis Pharmaceuticals
Investigators
Study Director: Novartis Pharmaceuticals Novartis Pharmaceuticals
  More Information

No publications provided

Responsible Party: Novartis ( Novartis Pharmaceuticals )
ClinicalTrials.gov Identifier: NCT01582061     History of Changes
Other Study ID Numbers: CSOM230B2406
Study First Received: April 12, 2012
Last Updated: March 22, 2013
Health Authority: United States: Food and Drug Administration
Brazil: Ethics Committee
Brazil: Ministry of Health
Czech Republic: Ethics Committee
Czech Republic: State Institute for Drug Control
Egypt: Institutional Review Board
Germany: Ethics Commission
Germany: Ministry of Health
Greece: Ethics Committee
Greece: Ministry of Health and Welfare
Lebanon: Institutional Review Board
Netherlands: Independent Ethics Committee
Netherlands: Medicines Evaluation Board (MEB)
Romania: National Medicines Agency
Russia: Ethics Committee
Russia: Ministry of Health of the Russian Federation
South Korea: Institutional Review Board
South Korea: Korea Food and Drug Administration (KFDA)
Spain: Ethics Committee
Spain: Ministry of Health
Thailand: Ethical Committee
Thailand: Food and Drug Administration

Keywords provided by Novartis:
Cushing's disease
Hormone disorder
Cortisol
Adrenocorticotropic hormone
Pituitary tumor

Additional relevant MeSH terms:
Cushing Syndrome
Pituitary ACTH Hypersecretion
Adrenocortical Hyperfunction
Adrenal Gland Diseases
Endocrine System Diseases
Hyperpituitarism
Pituitary Diseases
Hypothalamic Diseases
Brain Diseases
Central Nervous System Diseases
Nervous System Diseases
Adrenocorticotropic Hormone
Hormones
Hormones, Hormone Substitutes, and Hormone Antagonists
Physiological Effects of Drugs
Pharmacologic Actions

ClinicalTrials.gov processed this record on May 22, 2013