Study of Denufosol Inhalation Solution in Patients With Mild Cystic Fibrosis Lung Disease

This study has been completed.
Sponsor:
Information provided by:
Merck
ClinicalTrials.gov Identifier:
NCT00357279
First received: July 25, 2006
Last updated: March 30, 2011
Last verified: June 2008
  Purpose

The purpose of this trial is to evaluate the safety and effectiveness of a one dose strength of denufosol compared to placebo in patients with mild CF lung disease.


Condition Intervention Phase
Cystic Fibrosis
Drug: denufosol tetrasodium (INS37217) Inhalation Solution
Drug: Placebo - 0.9% w/v sodium chloride solution
Phase 3

Study Type: Interventional
Study Design: Allocation: Randomized
Intervention Model: Parallel Assignment
Masking: Double Blind (Subject, Investigator)
Primary Purpose: Treatment
Official Title: A Multi-Center, Double-Blind, Placebo-Controlled Randomized, Efficacy and Safety Study of Denufosol Tetrasodium (INS37217) Inhalation Solution in Patients With Mild Cystic Fibrosis Lung Disease

Resource links provided by NLM:


Further study details as provided by Merck:

Primary Outcome Measures:
  • Change in lung function [ Time Frame: 48 weeks ] [ Designated as safety issue: Yes ]

Secondary Outcome Measures:
  • Pulmonary exacerbation [ Time Frame: 48 weeks ] [ Designated as safety issue: Yes ]
  • Requirements for concomitant CF medications [ Time Frame: 48 weeks ] [ Designated as safety issue: No ]
  • Quality of Life [ Time Frame: 48 weeks ] [ Designated as safety issue: No ]

Estimated Enrollment: 350
Study Start Date: July 2006
Study Completion Date: September 2008
Primary Completion Date: September 2008 (Final data collection date for primary outcome measure)
Arms Assigned Interventions
Placebo Comparator: 1
Placebo
Drug: Placebo - 0.9% w/v sodium chloride solution
4.2 mL of solution, allowing delivery of approximately 4 mL into the nebulizer cup for nebulization, three times daily for six months.
Experimental: 2 Drug: denufosol tetrasodium (INS37217) Inhalation Solution
Denufosol 60 mg is administered as an inhalation solution, three times daily for six months during the double-blind portion of the study. Subsequently, denufosol 60 mg is administered for an additional six months during the open label safety extension.

  Eligibility

Ages Eligible for Study:   5 Years and older
Genders Eligible for Study:   Both
Accepts Healthy Volunteers:   No
Criteria

Inclusion Criteria:

  • Have confirmed diagnosis of cystic fibrosis
  • Have FEV1 of greater than or equal to 75% of predicted normal for age, gender, and height
  • Be able to reproducibly perform spirometry maneuvers
  • Be clinically stable for at least 4 weeks prior to screening

Exclusion Criteria:

  • Have abnormal renal or liver function
  • Have chest x-ray at screening suggesting clinically significant active pulmonary disease
  • Be colonized with Burkholderia cepacia
  • Have had a lung transplant
  Contacts and Locations
Please refer to this study by its ClinicalTrials.gov identifier: NCT00357279

  Hide Study Locations
Locations
United States, Alabama
Children's Hospital
Birmingham, Alabama, United States, 35233
University of Alabama at Birmingham Hospital and Clinics
Birmingham, Alabama, United States, 35249
United States, Alaska
Pediatric Breathing Disorders Clinic
Anchorage, Alaska, United States, 99508
Providence Alaska Medical Center
Anchorage, Alaska, United States, 99508
United States, Arizona
Phoenix Children's Hospital
Phoenix, Arizona, United States, 85016
United States, Arkansas
Arkansas Children's Hospital
Little Rock, Arkansas, United States, 72202
University of Arkansas for Medical Sciences
Little Rock, Arkansas, United States, 72205
United States, California
Childrens Hospital Los Angeles
Los Angeles, California, United States, 90027
Children'a Hospital and Research Center at Oakland
Oakland, California, United States, 94609
Children's Hospital of Orange County
Orange, California, United States, 92868
Children's Hospital of Orange County Pulmonary Clinic
Orange, California, United States, 92868
Capital Allergy and Respiratory Disease Center
Roseville, California, United States, 95661
Capital Allergy and Respiratory Disease Center
Sacramento, California, United States, 95819
UC Davis Medical Center
Sacramento, California, United States, 95817
Stanford University Hospital and Clinics
Stanford, California, United States, 94305-5236
United States, Colorado
The Children's Hospital
Denver, Colorado, United States, 80218
United States, Connecticut
Connecticut Children's Medical Center
Hartford, Connecticut, United States, 06106
Yale School of Medicine
New Haven, Connecticut, United States, 06520-8064
United States, Delaware
Alfred I. duPont Hospital for Children
Wilmington, Delaware, United States, 19803
United States, Florida
Shands at the University of Florida
Gainesville, Florida, United States, 32610
Nemours Children's Clinic
Jacksonville, Florida, United States, 32207
Miami Children's Hospital
Miami, Florida, United States, 33155
Nemours Children's Clinic
Orlando, Florida, United States, 32806
United States, Georgia
Emory Cystic Fibrosis Center
Atlanta, Georgia, United States, 30322
United States, Illinois
Children's Memorial Hospital
Chicago, Illinois, United States, 60614
Chicago CF Care Specialists/CFI
Glenview, Illinois, United States, 60025
Loyola University Medical Center Outpatient Center
Maywood, Illinois, United States, 60153
Oakbrook Terrace Medical Center
Oakbrook Terrace, Illinois, United States, 60181
United States, Indiana
James Whitcomb Riley Hospital for Children
Indianapolis, Indiana, United States, 46202
United States, Iowa
University of Iowa Hospitals and Clinics
Iowa City, Iowa, United States, 52242-1083
United States, Kansas
Via Christi Specialty Clinics/CR Clinic
Wichita, Kansas, United States, 67214
United States, Kentucky
University of Kentucky
Lexington, Kentucky, United States, 40536-0284
United States, Louisiana
Louisiana State University Health Sciences Center
Shreveport, Louisiana, United States, 71130
United States, Maine
Maine Medical Center
Portland, Maine, United States, 04102
United States, Maryland
Johns Hopkins Hospital
Baltimore, Maryland, United States, 21287
United States, Massachusetts
Massachusetts General Hospital
Boston, Massachusetts, United States, 02114
United States, Michigan
Spectrum Health Cystic Fibrosis Care Center
Grand Rapids, Michigan, United States, 49503
Michigan Medical PC
Grand Rapids, Michigan, United States, 49546
Pediatric Pulmonary Clinic
Grand Rapids, Michigan, United States, 49503
United States, Minnesota
The Minnesota CF Center
Minneapolis, Minnesota, United States, 55455
Univeristy of Minnesota
Minneapolis, Minnesota, United States, 55455
United States, Missouri
Cardinal Glennon Children's Medical Center
St. Louis, Missouri, United States, 63104
United States, Nebraska
University of Nebraska Medical Center
Omaha, Nebraska, United States, 68198
United States, Nevada
Childrens Lung Specialists, LTD
Las Vegas, Nevada, United States, 89107
United States, New Jersey
Saint Barnabas Ambulatory Care Center
Livingston, New Jersey, United States, 07039
The Respiratory Center for Children, Morristown Memorial Hospital
Morristown, New Jersey, United States, 07962
United States, New York
Women & Children's Hospital of Buffalo
Buffalo, New York, United States, 14222
Irving Goldman Family Care Center
Great Neck, New York, United States, 11021
Westchester Medical Center and New York Medical College
Hawthorne, New York, United States, 10532
The Cystic Fibrosis Center St. Vincent's Hospital, Manhattan
New York, New York, United States, 10011
Columbia University Medical Center
New York, New York, United States, 10032
University of Rochester
Rochester, New York, United States, 14642
SUNY Upstate Medical University Hospital
Syracuse, New York, United States, 13210
United States, North Carolina
University of North Carolina at Chapel Hill
Chapel Hill, North Carolina, United States, 27599
United States, Ohio
Cincinnati Children's Hospital Medical Center
Cincinnati, Ohio, United States, 45229
University Hospitals of Cleveland
Cleveland, Ohio, United States, 44106
Children's Hospital
Columbus, Ohio, United States, 43205
United States, Oklahoma
Santiago Reyes
Oklahoma City, Oklahoma, United States, 73112
United States, Oregon
Oregon Health and Sciences University, Hospital (OHSU)
Portland, Oregon, United States, 97239
United States, Pennsylvania
PHH Cystic Fibrosis Center
Harrisburg, Pennsylvania, United States, 17110
Penn State Milton S. Hershey Medical Center
Hershey, Pennsylvania, United States, 17033
The Childrens Hospital of Philadelphia
Philadelphia, Pennsylvania, United States, 19104
Children's Hospital of Pittsburgh
Pittsburgh, Pennsylvania, United States, 15213
United States, South Carolina
Pediatric Pulmonary Associates
Columbia, South Carolina, United States, 29203
United States, Texas
Children's Medical Center Dallas, Dallas Cystic Fibrosis Center
Dallas, Texas, United States, 75235
Baylor College of Medicine
Houston, Texas, United States, 77030
Texas Children's Hospital
Houston, Texas, United States, 77030
Alamo Clinical Research Associates
San Antonio, Texas, United States, 78212
The University of Texas Health Science Center at San Antonia
San Antonio, Texas, United States, 78229-3900
United States, Utah
University of Utah
Salt Lake City, Utah, United States, 84132
United States, Virginia
University of Virginia Health System
Charlottesville, Virginia, United States, 22908
Primary Care Center
Charlottesville, Virginia, United States, 22908
Kluge Children's Rehabilitation Center
Charlottesville, Virginia, United States, 22903
Naval Medical Center Portsmouth
Portsmouth, Virginia, United States, 23708
Virginia Commonwealth University Pediatric Pulmonary Clinic
Richmond, Virginia, United States, 23219
Virginia Commonwealth University Children's Pavilion
Richmond, Virginia, United States, 23219
United States, Washington
Childrens Hospital and Regional Medical Center
Seattle, Washington, United States, 98105
University of Washington Medical Center
Seattle, Washington, United States, 98195
United States, Wisconsin
University of Wisconsin Hospital and Clinics
Madison, Wisconsin, United States, 53792
Canada, British Columbia
British Columbia's Children's Hospital
Vancouver, British Columbia, Canada, V6H-3V4
Canada, Nova Scotia
Queen Elizabeth II Health Sciences Center
Halifax, Nova Scotia, Canada, B3H 3A7
Sponsors and Collaborators
Merck
  More Information

No publications provided by Merck

Additional publications automatically indexed to this study by ClinicalTrials.gov Identifier (NCT Number):
Responsible Party: Amy Schaberg, RN, BSN Vice President Respiratory Clinical Research, Inspire Pharmaceuticals
ClinicalTrials.gov Identifier: NCT00357279     History of Changes
Other Study ID Numbers: 08-108
Study First Received: July 25, 2006
Last Updated: March 30, 2011
Health Authority: United States: Food and Drug Administration

Additional relevant MeSH terms:
Cystic Fibrosis
Fibrosis
Lung Diseases
Pulmonary Fibrosis
Pancreatic Diseases
Digestive System Diseases
Respiratory Tract Diseases
Genetic Diseases, Inborn
Infant, Newborn, Diseases
Pathologic Processes

ClinicalTrials.gov processed this record on May 23, 2013