Noninvasive Ventilation in ALS Patients With Mild Respiratory Involvement

This study has been completed.
Sponsor:
Collaborator:
Information provided by:
Johns Hopkins University
ClinicalTrials.gov Identifier:
NCT00386464
First received: October 10, 2006
Last updated: November 8, 2007
Last verified: April 2007

October 10, 2006
November 8, 2007
April 2002
Not Provided
Decline in forced vital capacity
Same as current
Complete list of historical versions of study NCT00386464 on ClinicalTrials.gov Archive Site
  • quality of life
  • respiratory quality of life
Same as current
Not Provided
Not Provided
 
Noninvasive Ventilation in ALS Patients With Mild Respiratory Involvement
Noninvasive Ventilation in ALS Patients With Mild Respiratory Involvement

Non-invasive ventilation or BiPAP®, which is a form of breathing support delivered through a facemask, is a successful treatment for the respiratory complications of amyotrophic lateral sclerosis (ALS). It has been shown to prolong survival, improve quality of life, and improve cognitive function. It is widely used among patients with ALS who have advanced breathing difficulties. It is not known whether there is benefit to using non-invasive ventilation earlier in the disease course.

There is evidence that non-invasive ventilation may slow down the decline in breathing function. If this were true then it would make sense to start non-invasive ventilation use earlier than the current clinically accepted practices.

The purpose of this study is to determine whether using non-invasive ventilation early in the course of disease can slow the decline in breathing function.

Patients remain in the study for 6 months and are asked to make 7 clinic visits during which time they will undergo pulmonary function tests and complete questionnaires.

This is a randomized, crossover trial for patient with ALS and mild respiratory involvement. Patients with forced vital capacity above 60% of the predicted value can join. Patients will be assigned to either start using non-invasive ventilation at night or continue their usual care. After three months, patients will switch over to the other treatment group. For example, a patient who was initially assigned to continue their usual care would begin using non-invasive ventilation after three months.

Interventional
Phase 2
Phase 3
Allocation: Randomized
Endpoint Classification: Safety/Efficacy Study
Intervention Model: Crossover Assignment
Masking: Open Label
Primary Purpose: Supportive Care
Amyotrophic Lateral Sclerosis
Device: noninvasive positive pressure ventilation
Not Provided
Not Provided

*   Includes publications given by the data provider as well as publications identified by ClinicalTrials.gov Identifier (NCT Number) in Medline.
 
Completed
60
September 2007
Not Provided

Inclusion Criteria:

  • Probable or definite ALS by El Escorial criteria
  • age >17 years
  • FVC >60
  • minimal respiratory symptoms (no orthopnea or dyspnea at rest)
  • ability to provide informed consent

Exclusion Criteria:

  • Presence of another neurodegenerative disease
  • arterial CO2 above 45 mmHg
  • O2 below 60 mmHg
  • coexisting chronic lung disease unrelated to ALS
  • presence of an unstable medical condition such as coronary artery disease, liver failure, renal failure or cancer in the 30 days preceding enrollment
Both
18 Years and older
No
Contact information is only displayed when the study is recruiting subjects
United States
 
NCT00386464
HL 67887-03
No
Not Provided
Johns Hopkins University
National Heart, Lung, and Blood Institute (NHLBI)
Principal Investigator: Noah Lechtzin, MD Johns Hopkins University
Study Chair: Charles M Wiener, MD Johns Hopkins University
Johns Hopkins University
April 2007

ICMJE     Data element required by the International Committee of Medical Journal Editors and the World Health Organization ICTRP